
▲ 65 r/biotech
Regenxbio says Duchenne gene therapy succeeded in clinical trial, paving way for FDA submission
Regenxbio announced positive results from their Duchenne muscular dystrophy gene therapy trial, showing sufficient levels of a key protein. This success is a significant step towards submitting the therapy to the FDA for approval and aims to offer a safer, more effective alternative to existing treatments, which have faced safety concerns
u/Sad-Watercress-2240 — 17 hours ago